FDA Approves First-Ever Gene Therapy for Treatment of Genetic Hearing Loss | Hacker News

The FDA approved the first gene therapy for a rare genetic hearing-loss subtype.

The treatment targets OTOF-related inherited deafness and was reviewed through an accelerated rare-disease pathway.

The decision marks a milestone for precision treatment in a small patient group.

It also highlights how fast-track regulatory programs can bring niche therapies to patients sooner.